Center for Motor Neuron Biology and Disease
![The Motor Neuron Center Logo](https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_40_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=MIrfaHTP 40w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_200_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=0oVrj56x 200w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_260_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=BXzzEKz3 260w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_320_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=HCDxOCoA 320w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_400_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=OEYOPTT8 400w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_520_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=SBDdntaf 520w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_640_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=c6SSLWtT 640w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_800_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=Zt9ZYA-D 800w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_1040_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=4jiaOUEa 1040w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_1280_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=2ol7FuXe 1280w, https://www.vagelos.columbia.edu/sites/default/files/styles/cola_media_1600_3_1/public/media/images/2022-08/mnc-banner-no-text.jpg?itok=if1_IFc5 1600w)
Motor Neuron Center
Columbia’s Motor Neuron Center will transform our understanding of human health. For the first time, brilliant scientific minds are working together in a common approach to currently incurable motor neuron diseases: spinal muscular atrophy (SMA) in children and amyotrophic lateral sclerosis (ALS; Lou Gehrig’s disease) in adults. New discoveries in the field of motor neuron biology will fuel the search for effective therapy for patients.
News
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Haploinsufficiency of the SLC2A1 gene and paucity of its translated product, the glucose transporter-1 (Glut1) protein, disrupt brain function and cause the neurodevelopmental disorder...
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Behavioral deficits in neurodegenerative diseases are often attributed to the selective dysfunction of vulnerable neurons via cell-autonomous mechanisms.
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The RNA-binding protein FUS participates in several RNA biosynthetic processes and has been linked to the pathogenesis of amyotrophic lateral sclerosis (ALS) and frontotemporal dementia.
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Research
Support the Center
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Your support of Columbia’s Motor Neuron Center will benefit patients and their families through earlier diagnosis, improved patient care, and the discovery of novel treatments.